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Development and Clinical Translation of Approved Gene Therapy Products for Genetic Disorders

25 Sept 2019

Abstract excerpt

The field of gene therapy is striving more than ever to define a path to the clinic and the market. Twenty gene therapy products have already been approved and over two thousand human gene therapy clinical trials have been reported world-wide. These advances raise great hope to treat devastating rare and inherited diseases as well as intractable illnesses. Gene therapy is presently starting to become commercially...

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PMID: 31608113
DOI: 10.3389/fgene.2019.00868

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