Article
Gene therapy for heart failure and cardiomyopathies.
Revista espanola de cardiologia (English ed.) - 1 Dec 2023
Argirò Alessia, Ding Jeffrey, Adler Eric
Abstract excerpt
Gene therapy strategies encompass a range of approaches, including gene replacement and gene editing. Gene replacement involves providing a functional copy of a modified gene, while gene editing allows for the correction of existing genetic mutations. Gene therapy has already received approval for treating genetic disorders like Leber's congenital amaurosis and spinal muscular atrophy. Currently, research is...
Read the complete abstract on PubMedTopics
Share this publication in a Topic to start or enrich a Post.
