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Article

Overcoming the Challenges to Clinical Development of X-Linked Retinitis Pigmentosa Therapies: Proceedings of an Expert Panel.

Translational vision science & technology - 1 Jun 2023

Birch David G, Cheetham Janet K, Daiger Stephen P, Hoyng Carel, Kay Christine, MacDonald Ian M, Pennesi Mark E, Sullivan Lori S

Abstract excerpt

X-linked retinitis pigmentosa (XLRP) is a rare inherited retinal disease manifesting as impaired night vision and peripheral vision loss that progresses to legal blindness. Although several trials of ocular gene therapy for XLRP have been conducted or are in progress, there is currently no approved treatment. In July 2022, the Foundation Fighting Blindness convened an expert panel to examine relevant research and...

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Identifiers

PMID: 37294701
DOI: 10.1167/tvst.12.6.5
PMCID: PMC10270308

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