Article
An update on the US adult thalassaemia population: a report from the CDC thalassaemia treatment centres.
British journal of haematology - 1 Jan 2022
Chapin John, Cohen Alan R, Neufeld Ellis J, Vichinsky Elliott, Giardina Patricia J, Boudreaux Jeanne, Le Binh C, Kenney Kristy, Trimble Sean, Thompson Alexis A
Abstract excerpt
Thalassaemia is caused by genetic globin defects leading to anaemia, transfusion-dependence and comorbidities. Reduced survival and systemic organ disease affect transfusion-dependent thalassaemia major and thalassaemia intermedia. Recent improvements in clinical management have reduced thalassaemia mortality. The therapeutic landscape of thalassaemia may soon include gene therapies as functional cures. An...
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