Discover Community Create You

Loading publication...

Noodle always counts identifier-free feature events for service operation. With your permission, Google Analytics can also estimate audience and engagement. Search text, publication identifiers, cookies, IP addresses and browser fingerprints are never included in Noodle's first-party event counters.

Privacy details

Article

Patient preferences for gene therapy in haemophilia: Results from the PAVING threshold technique survey

1 Sept 2021

Abstract excerpt

OBJECTIVES: The aim of the Patient preferences to Assess Value IN Gene therapies (PAVING) study was to investigate trade-offs that adult Belgian people with haemophilia (PWH) A and B are willing to make when choosing between prophylactic factor replacement therapy (PFRT) and gene therapy. METHODS: The threshold technique was used to quantify the minimum acceptable benefit (MAB) of a switch from PFRT to gene...

Read the complete abstract on PubMed

Topics

Share this publication in a Topic to start or enrich a Post.

Share to Hemophilia Treatment and Research
Share to Neurogenetic and Muscular Disorders Research
Share to Virus-based gene therapy research

Methodology Data sources Editorial policy Privacy About Contact Helena Bioinformatics

Source

Identifiers

PMID: 34472162
DOI: 10.1111/hae.14401

Provenance

PubMed metadata and Literature Corpus relationships. Corpus snapshot updated 5 Sept 2026.

Related research

Semantic proximity does not establish scientific evidence.

Research trail→

Click a neighbor to travelStep 1 · 12 closest

Patient preferences for gene therapy in haemophilia: Results from the PAVING threshold technique surveyPMID 34472162Read ↗

Preferences and health utilities related to disease and treatment features for patients with hemophilia A in CanadaSemantic proximity Read ↗

Patient, consumer and societal values, perceptions and preferences on high-cost gene therapiesSemantic proximity Read ↗

Public perception and willingness to accept somatic gene therapy: A Belgian survey studySemantic proximity Read ↗

Perspectives and perception of haemophilia gene therapy by French patientsSemantic proximity Read ↗

The 1st WFH Gene Therapy Round Table: Understanding the landscape and challenges of gene therapy for haemophilia around the worldSemantic proximity Read ↗

Public perceptions and willingness to accept somatic gene therapy: A Belgian survey studySemantic proximity Read ↗

Gene therapy in hemophilia A: a cost-effectiveness analysisSemantic proximity Read ↗

Economic evaluation of a novel genetic screening test for risk of venous thromboembolism compared with standard of care in women considering combined hormonal contraception in Switzerland.Semantic proximity Read ↗

Development of a haemophilia A gene therapy shared decision‐making tool for cliniciansSemantic proximity Read ↗

Preferences for genetic interventions for SCA and Huntington’s disease: results of a discrete choice experiment among patients.Semantic proximity Read ↗

Post-operative anticoagulation therapy after knee or hip replacement: The role of patients’ preferences in selection of therapySemantic proximity Read ↗

The quality of life associated with prophylactic treatments for women with BRCA1/2 mutations.Semantic proximity Read ↗

⌁Select a neighboring publication to make it the new centre.