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Surgical Aspects in Gene Therapy for Inherited Retinal Diseases.

Klinische Monatsblatter fur Augenheilkunde - 1 Mar 2021

Fischer M Dominik, Bartz-Schmidt Karl Ulrich, Dimopoulos Spyridon, Herrmann Philipp, Gerhardt Maximilian, Holz Frank G, Priglinger Siegfried

Abstract excerpt

Inherited retinal dystrophies (IRD) have been studied since their recognition by Franz Donders and Albrecht von Graefe. It nevertheless took 100 years for a causal therapy to take shape in the form of gene therapy: The approval of Voretigen Neparvovec (VN) for the treatment of hereditary retinal dystrophies due to RPE65 mutations was thus a significant milestone - for the era of personalised medicine in general...

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PMID: 33618387
DOI: 10.1055/a-1315-1331

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PubMed metadata and Literature Corpus relationships. Corpus snapshot updated 6 Sept 2026. Manifest publication-graph-cohort-2026-09-06.1.

Source receipt: pubmed, retrieved 6 Sept 2026.

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