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Article

Progress in Gene Therapy for Rhodopsin Autosomal Dominant Retinitis Pigmentosa.

Advances in experimental medicine and biology - 1 Jan 2019

Sudharsan Raghavi, Beltran William A

Abstract excerpt

This brief review summarizes the major proof-of-concept gene therapy studies for autosomal dominant retinitis pigmentosa (RP) caused by mutations in the rhodopsin gene (RHO-adRP) that have been conducted over the past 20 years in various animal models. We have listed in tabular form the various approaches, gene silencing reagents, gene delivery strategies, and salient results from these studies.

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Methodology Data sources Editorial policy Privacy About Contact Helena Bioinformatics

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Identifiers

PMID: 31884598
DOI: 10.1007/978-3-030-27378-1_19
PMCID: PMC7217593

Provenance

PubMed metadata and Literature Corpus relationships. Corpus snapshot updated 6 Sept 2026. Manifest publication-graph-cohort-2026-09-06.1.

Source receipt: pubmed, retrieved 6 Sept 2026.

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