Article
Gene therapy for primary immunodeficiency
8 Jul 2019
Abstract excerpt
Gene therapy is now being trialled as a therapeutic option for an expanding number of conditions, based primarily on the successful treatment over the past two decades of patients with specific primary immunodeficiencies (PIDs) including severe combined immunodeficiency and Wiskott-Aldrich syndrome and metabolic conditions such as leukodystrophy. The field has evolved from the use of gammaretroviral vectors to...
Read the complete abstract on PubMedTopics
Share this publication in a Topic to start or enrich a Post.
