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Article

Current and emerging treatment options for Wiskott-Aldrich syndrome.

Expert review of clinical immunology - 1 Jan 2015

Worth Austen J J, Thrasher Adrian J

Abstract excerpt

Wiskott-Aldrich syndrome is a life-threatening primary immunodeficiency associated with a bleeding tendency, eczema and a high incidence of autoimmunity and malignancy. Stem cell transplantation offers the opportunity of cure for all these complications, and over the past 35 years there has been a remarkable improvement in survival following this treatment. Here, we review advances in management of clinical...

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Identifiers

PMID: 26159751
DOI: 10.1586/1744666X.2015.1062366

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