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Article

Outcome in six children with mucopolysaccharidosis type IH, Hurler syndrome, after haematopoietic stem cell transplantation (HSCT).

Acta paediatrica (Oslo, Norway : 1992) - 1 Aug 2008

Malm Gunilla, Gustafsson Britt, Berglund Gunilla, Lindström Maria, Naess Karin, Borgström Birgit, von Döbeln Ulrika, Ringdén Olle

Abstract excerpt

AIM: To follow-up six children with severe mucopolysaccharidosis type IH, Hurler syndrome, who were treated before 24 months of age with haematopoietic stem cell transplantation. METHODS: In Sweden, during the last 10-year period, six consecutive children born with severe mucopolysaccharidoses type IH have been successfully transplanted using matched unrelated donors between the ages of 11 and 24 months (mean age...

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Identifiers

PMID: 18452566
DOI: 10.1111/j.1651-2227.2008.00811.x

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PubMed metadata and Literature Corpus relationships. Corpus snapshot updated 7 Sept 2026. Manifest publication-graph-cohort-2026-09-07.1.

Source receipt: pubmed, retrieved 7 Sept 2026.

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