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Article

Correction of the murine Wiskott-Aldrich syndrome phenotype by hematopoietic stem cell transplantation.

Blood - 15 Jun 2002

Strom Ted S, Li Xiuling, Cunningham John M, Nienhuis Arthur W

Abstract excerpt

Allogeneic hematopoietic stem cell transplantation (HSCT) corrects the Wiskott-Aldrich syndrome (WAS) phenotype. However, the toxicity and mortality frequently associated with this approach warrant the exploration of new therapeutic strategies. Transplantation studies of a murine model of WAS deficiency have been limited by the occurrence of a radiation-induced fatal exacerbation of a pre-existing colitis in the...

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Identifiers

PMID: 12036897
DOI: 10.1182/blood-2001-12-0319

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PubMed metadata and Literature Corpus relationships. Corpus snapshot updated 7 Sept 2026. Manifest publication-graph-cohort-2026-09-07.1.

Source receipt: pubmed, retrieved 7 Sept 2026.

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Correction of the murine Wiskott-Aldrich syndrome phenotype by hematopoietic stem cell transplantation.PMID 12036897Read ↗

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