Gene-based therapies for hemophilia

doi:10.1016/j.rpth.2025.102870

Loading publication...

Noodle always counts identifier-free feature events for service operation. With your permission, Google Analytics can also estimate audience and engagement. Search text, publication identifiers, cookies, IP addresses and browser fingerprints are never included in Noodle's first-party event counters.

Privacy details

Topics Community

Back to search

Article

Gene-based therapies for hemophilia

25 Apr 2025

Abstract excerpt

Gene therapy is a transformative approach to treating genetic disorders in order to improve disease outcomes for patients. Hemophilia A and B are inherited genetic disorders caused by mutations in the FVIII and FIX genes, respectively. Traditional treatments for hemophilia have included intravenous plasma, factor concentrates, and nonfactor therapies that require lifelong prophylaxis and carry risks of factor...

Source

Open in PubMed

Identifiers

PMID: 40488175
DOI: 10.1016/j.rpth.2025.102870

Provenance

PubMed metadata and Literature Corpus relationships. Corpus snapshot updated 31 Aug 2026.

Methodology Data sources Editorial policy Privacy About Contact Helena Bioinformatics

Community interpretation

Discuss the evidence

Ask a question, add context or challenge an interpretation. Community activity is separate from scientific evidence strength.

discussions

replies

Citations encouraged

Claims remain attributable.

No discussion yet

Be the first to add a careful, cited interpretation.

Related research

Semantic proximity does not establish scientific evidence.

Research trail→

Click a neighbor to travelStep 1 · 12 closest

Gene-based therapies for hemophiliaPMID 40488175Read ↗

Advances in Gene Therapy for HemophiliaSemantic proximity Read ↗

Etranacogene dezaparvovec for hemophilia B gene therapySemantic proximity Read ↗

The Arrival of Gene Therapy for Patients with Hemophilia ASemantic proximity Read ↗

Gene therapy for hemophiliaSemantic proximity Read ↗

Gene therapy strategies for hemophilia: benefits versus risksSemantic proximity Read ↗

Gene therapy in hemophilia: the dawn of a new eraSemantic proximity Read ↗

Hemophilia gene therapy comes of ageSemantic proximity Read ↗

Gene Therapy for Inherited Bleeding DisordersSemantic proximity Read ↗

Advances and challenges for hemophilia gene therapySemantic proximity Read ↗

Gene therapy for hemophiliaSemantic proximity Read ↗

Hemophilia gene therapy comes of ageSemantic proximity Read ↗

⌁Select a neighboring publication to make it the new centre.