Current clinical applications of AAV-mediated gene therapy

Abstract excerpt

Currently, there are an estimated 8,000 genetic disorders that cumulatively affect approximately 10% of the population. Even among the 5% of patients with genetic disease that have treatment options, these therapeutics rarely address the underlying cause of disease but rather focus on managing or modifying symptoms and typically require recurrent, lifelong therapy. A therapeutic approach to genetic disease that...

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• Herpesvirus Infections and Treatments
• Viral Infections and Immunology Research
• Virus-based gene therapy research