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Article

Peptide-based therapeutics targeting genetic disorders.

Drug discovery today - 1 Dec 2024

Subramanian Shweta, Jain Meenakshi, Misra Rajkumar, Jain Rahul

Abstract excerpt

Genetic disorders (GDs) are challenging to treat owing to a lack of optimal treatment regimens and intricate and often difficult-to-understand underlying biological processes. Limited therapeutic approaches, which mostly provide symptomatic relief, are available. To date, a limited number of peptide-based drugs for the treatment of GDs are available, and several candidates are under clinical study. This review...

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PMID: 39419376
DOI: 10.1016/j.drudis.2024.104209

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PubMed metadata and Literature Corpus relationships. Corpus snapshot updated 7 Sept 2026.

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