Article
Genetic therapies in cystic fibrosis.
Current opinion in pulmonary medicine - 1 Nov 2023
Taylor-Cousar Jennifer L, Boyd A Christopher, Alton Eric W F W, Polineni Deepika
Abstract excerpt
PURPOSE OF REVIEW: Advances in cystic fibrosis (CF) therapies over the past decade pivotally changed the morbidity and mortality of CF with the advent of cystic fibrosis transmembrane conductance regulator (CFTR) modulators that rescue dysfunctional CFTR protein in individuals with eligible genotypes. However, a significant proportion of the CF population is in need of alternative treatment strategies to address...
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