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Article

Decision-making and challenges within the evolving treatment algorithm in spinal muscular atrophy: a clinical perspective.

Expert review of neurotherapeutics - 1 Jan 2000

Balaji Lakshmi, Farrar Michelle A, D'Silva Arlene M, Kariyawasam Didu S

Abstract excerpt

INTRODUCTION: The clinical application of disease modifying therapies has dramatically changed the paradigm of the management of people with spinal muscular atrophy (SMA), from sole reliance on symptomatic care directed toward the downstream consequences of muscle weakness, to proactive intervention and even preventative care. AREAS COVERED: In this perspective, the authors evaluate the contemporary therapeutic...

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PMID: 37227306
DOI: 10.1080/14737175.2023.2218549

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