Loading publication...

Noodle always counts identifier-free feature events for service operation. With your permission, Google Analytics can also estimate audience and engagement. Search text, publication identifiers, cookies, IP addresses and browser fingerprints are never included in Noodle's first-party event counters.

Privacy details

Article

Gene therapy for sickle cell disease: where we are now?

10 Dec 2021

Abstract excerpt

The landscape of sickle cell disease (SCD) treatment continues to evolve rapidly, with new disease-modifying therapies in development and potentially curative options on the horizon. Until recently, allogeneic stem cell transplant has been the only proven cure for SCD. Gene therapy is rising to the forefront of the discussion as a potentially curative or highly disease- modifying option for abating the...

Read the complete abstract on PubMed

Topics

Share this publication in a Topic to start or enrich a Post.

Share to Hemoglobinopathies and Related Disorders
Share to Iron Metabolism and Disorders
Share to Prenatal Screening and Diagnostics

Methodology Data sources Editorial policy Privacy About Contact Helena Bioinformatics

Source

Identifiers

PMID: 34889358
DOI: 10.1182/hematology.2021000250

Provenance

PubMed metadata and Literature Corpus relationships. Corpus snapshot updated 2 Sept 2026.

Related research

Semantic proximity does not establish scientific evidence.

Research trail→

Click a neighbor to travelStep 1 · 12 closest

Gene therapy for sickle cell disease: where we are now?PMID 34889358Read ↗

Treating Sickle Cell Disease: Gene Therapy ApproachesSemantic proximity Read ↗

Current state of gene therapy in sickle cell diseaseSemantic proximity Read ↗

Promise of gene therapy to treat sickle cell diseaseSemantic proximity Read ↗

Gene therapy for sickle cell disease: moving from the bench to the bedsideSemantic proximity Read ↗

Diverse Approaches to Gene Therapy of Sickle Cell DiseaseSemantic proximity Read ↗

Current and future treatments for sickle cell disease: From hematopoietic stem cell transplantation to in vivo gene therapySemantic proximity Read ↗

Gene therapy for sickle cell disease: An updateSemantic proximity Read ↗

The potential of gene therapy approaches for the treatment of hemoglobinopathies: achievements and challengesSemantic proximity Read ↗

Gene Therapy: A New Hope in Sickle Cell Disease TreatmentSemantic proximity Read ↗

Advances in Gene Therapy for Sickle Cell Disease: From Preclinical Innovations to Clinical Implementation and Access ChallengesSemantic proximity Read ↗

Sickle Cell Disease: From Genetics to Curative ApproachesSemantic proximity Read ↗

Defining curative endpoints for sickle cell disease in the era of gene therapy and gene editingSemantic proximity Read ↗

⌁Select a neighboring publication to make it the new centre.