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The Promise and the Hope of Gene Therapy

24 Mar 2021

Abstract excerpt

It has been over 30 years since visionary scientists came up with the term "Gene Therapy," suggesting that for certain indications, mostly monogenic diseases, substitution of the missing or mutated gene with the normal allele via gene addition could provide long-lasting therapeutic effect to the affected patients and consequently improve their quality of life. This notion has recently become a reality for certain...

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PMID: 34713249
DOI: 10.3389/fgeed.2021.618346

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