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Haemophilia, state of the art and new therapeutic opportunities, a regulatory perspective

27 Mar 2021

Abstract excerpt

Haemophilia A and B are rare bleeding disorders. Over the past decades, they have been transformed from debilitating diseases to manageable conditions in the Western world. However, optimizing haemophilia care remains challenging in developing countries. Several challenges and unmet needs remain in the treatment of the haemophilia limiting the QoL of patients. These challenges are now being addressed by extended...

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Methodology Data sources Editorial policy Privacy About Contact Helena Bioinformatics

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PMID: 33772837
DOI: 10.1111/bcp.14838

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