Article
Demographics and patient characteristics of 1209 patients with Gaucher disease: Descriptive analysis from the Gaucher Outcome Survey (GOS).
American journal of hematology - 1 Feb 2018
Zimran Ari, Belmatoug Nadia, Bembi Bruno, Deegan Patrick, Elstein Deborah, Fernandez-Sasso Diego, Giraldo Pilar, Goker-Alpan Ozlem, Lau Heather, Lukina Elena, Panahloo Zoya, Schwartz Ida Vanessa D
Abstract excerpt
The Gaucher Outcome Survey (GOS) is an international Gaucher disease (GD) registry established in 2010 for patients with a confirmed GD diagnosis, regardless of GD type or treatment status, designed to evaluate the safety and long-term effectiveness of velaglucerase alfa and other GD-related treatments. As of February 25, 2017, 1209 patients had enrolled, the majority from Israel (44.3%) and the US (31.4%)....
Read the complete abstract on PubMedTopics
Share this publication in a Topic to start or enrich a Post.