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Article

Emerging therapies for inherited retinal degeneration.

Science translational medicine - 7 Dec 2016

Scholl Hendrik P N, Strauss Rupert W, Singh Mandeep S, Dalkara Deniz, Roska Botond, Picaud Serge, Sahel José-Alain

Abstract excerpt

Inherited retinal degenerative diseases, a genetically and phenotypically heterogeneous group of disorders, affect the function of photoreceptor cells and are among the leading causes of blindness. Recent advances in molecular genetics and cell biology are elucidating the pathophysiological mechanisms underlying these disorders and are helping to identify new therapeutic approaches, such as gene therapy, stem...

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Identifiers

PMID: 27928030
DOI: 10.1126/scitranslmed.aaf2838

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PubMed metadata and Literature Corpus relationships. Corpus snapshot updated 7 Sept 2026. Manifest publication-graph-cohort-2026-09-08.1.

Source receipt: pubmed, retrieved 7 Sept 2026.

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